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Renewal of EAMS scientific opinion issued to Santhera Pharmaceuticals for Raxone to treat the decline of respiratory function in patients with Duchenne Muscular Dystrophy, including the public assessment report.
EAMS scientific opinion issued to Roche Products Limited for Risdiplam 0.75 mg/ml powder for oral solution in the treatment of type 1 and type 2 Spinal Muscular Atrophy (SMA) in patients 2 months and older who are not suitable for...
Funding will improve access for people who cannot use standard accessible toilets and their carers.
Employment Tribunal decision.
Advise patients and their caregivers to seek urgent medical attention if any signs or symptoms of communicating hydrocephalus develop during nusinersen therapy for spinal muscular atrophy. Patients with communicating hydrocephalus may require treatment with a cerebrospinal fluid (CSF) shunt.
A year on from a Ministerial review that confirmed the importance of Summary Care Records patient groups are advocating its use
First published during the 2010 to 2015 Conservative and Liberal Democrat coalition government
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